Neurocrine Biosciences explores new CAH treatments

Published 01/08/2025, 08:45 AM
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SAN DIEGO - Neurocrine (NASDAQ:NBIX) Biosciences, Inc. (NASDAQ:NBIX), a biopharmaceutical company with a market capitalization of $13.93 billion and impressive revenue growth of 25.72% over the last twelve months, has shared insights on the challenges of treating classic congenital adrenal hyperplasia (CAH) with traditional glucocorticoids (GCs) and the promise of new non-GC therapies. According to InvestingPro analysis, the company maintains a strong financial health score of "GREAT" and appears undervalued at current market prices. The narrative review, recently published in Expert Review of Endocrinology & Metabolism, discusses how novel treatments could enable lower, more physiologic dosing of GCs, potentially reducing the risk of long-term complications associated with high-dose GC treatments.

CAH is a lifelong condition that requires careful management of excess adrenocorticotropic hormone (ACTH) and androgens, historically controlled with high doses of GCs. These high doses, however, can lead to severe health issues, including cardiovascular, metabolic, and skeletal complications, as well as negative impacts on mental health and quality of life.

The review highlights the potential of new CAH medications that control excess ACTH and adrenal androgens through non-GC mechanisms, allowing for reduced glucocorticoid dosing. "The cumulative reduction over time translates into a significant decrease in the risk for complications," said Dr. Irina Bancos of the Mayo Clinic. With a robust gross profit margin of 68.07% and strong cash flows, the company is well-positioned to advance its therapeutic developments. For detailed financial analysis and additional insights, investors can access the comprehensive Pro Research Report available on InvestingPro, which covers over 1,400 US equities.

One such medication, CRENESSITY™ (crinecerfont), has been FDA-approved as an adjunctive treatment to control androgens in CAH patients aged four and above. CRENESSITY is the first CAH treatment that directly reduces excess ACTH and downstream adrenal androgen production, facilitating GC dose reduction.

CRENESSITY comes in capsule and oral solution forms, with dosages tailored for adults and pediatric patients based on body weight. It is to be taken with a meal and in conjunction with continued GC therapy for cortisol replacement.

Neurocrine Biosciences emphasizes the importance of this development for individuals with CAH and their families, as well as healthcare providers. The new treatment options represent an advancement in addressing the unmet needs in CAH therapy.

The information in this article is based on a press release statement from Neurocrine Biosciences, Inc. InvestingPro subscribers have access to 11 additional ProTips and extensive financial metrics that provide deeper insights into the company's performance and growth potential. The platform's Fair Value analysis suggests the stock may present an attractive investment opportunity at current levels.

In other recent news, Neurocrine Biosciences has been in the spotlight due to the launch of its new drug, Crenessity, which treats congenital adrenal hyperplasia (CAH). The company's impressive 25.7% revenue growth over the past year and a robust gross profit margin of 68% have further solidified its strong financial health. Piper Sandler has reiterated an Overweight stock rating for Neurocrine Biosciences, with a price target of $160.00, reflecting confidence in the company's financial outlook and the market potential of Crenessity.

The pricing for Crenessity has been set with two tiers, one for adults and adolescents and a lower one for pediatric patients. Piper Sandler's analysis forecasts that Crenessity's peak U.S. sales could reach between $800 million and $1 billion. BofA Securities has also shown confidence in Neurocrine Biosciences, projecting fiscal year 2025 sales of $39.4 million for Crenessity and raising the price target for the company to $182.

These recent developments highlight the company's commitment to developing effective treatments for neurological and endocrine-related diseases and disorders. Analysts from firms such as Goldman Sachs and H.C. Wainwright have maintained their Buy ratings on Neurocrine Biosciences, further endorsing the company's growth trajectory in the biopharmaceutical market.

This article was generated with the support of AI and reviewed by an editor. For more information see our T&C.

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